First Ever Drug for PKU
December 15, 2007 by MedHeadlines
Filed under Children's Health, Genetic Diseases
Med Headlines - Phenylketonuria (PKU) is a genetic disorder that can lead to impaired neurological function causing mental retardation and seizures. Although it is one of a very few genetic disorders controlled by diet, dietary restrictions are dramatic and must be started soon after birth. Unfortunately, until now, there have been no drugs given approval by the US Food and Drug Administration (FDA) for treatment of PKU. Read more





